Полина Степенски

Научные публикации

• Outcomes of allogeneic haematopoietic cell transplantation for myelofibrosis in children and adolescents: the retrospective study of the EBMT Paediatric Diseases WP
• Wiskott-Aldrich Syndrome: A study on 577 patients defining the genotype as a predictive biomarker for disease severity
• Development and Validation of a Prediction Model of Outcome After B-Cell Maturation Antigen-Directed Chimeric Antigen Receptor T-Cell Therapy in Relapsed/Refractory Multiple Myeloma
• Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiency
• Management of Atopy with Dupilumab and Omalizumab in CADINS Disease
• Combined Immunodeficiency Caused by a Novel Nonsense Mutation in LCK
• Chronic graft-versus-host disease detected by tissue-specific cell-free DNA methylation biomarkers
• Mesenchymal Stromal Cell-Derived Small Extracellular Vesicles Modulate Apoptosis, TNF Alpha and Interferon Gamma Response Gene mRNA Expression in T Lymphocytes
• Tumor-infiltrating lymphocyte transfusion in a patient with treatment refractory triple negative breast cancer
• Sclerotic-Type Cutaneous Chronic Graft-Versus-Host Disease Exhibits Activation of T Helper 1 and OX40 Cytokines
• High rate of adenovirus detection in gastrointestinal biopsies of symptomatic stem cell transplant recipients
• Clonal Myeloid Dysplasia Following CAR T-Cell Therapy: Chicken or the Egg?
• Risk and promise: an 11-year, single-center retrospective study of severe acute GVHD in pediatric patients undergoing allogeneic HSCT for nonmalignant diseases
• Long-Term Results with Thiotepa-Containing Conditioning Regimens for Autologous Stem Cell Transplantation
• Defibrotide plus best standard of care compared with best standard of care alone for the prevention of sinusoidal obstruction syndrome (HARMONY): a randomised, multicentre, phase 3 trial
• Response rates of extra-nodal diffuse large B cell lymphoma to anti-CD19-CAR T cells: A real word retrospective multicenter study
• Outcome of haematopoietic cell transplantation in children with lysosomal acid lipase deficiency: a study on behalf of the EBMT Inborn Errors Working Party
• SURVIVAL OF PEDIATRIC PATIENTS WITH NON-MALIGNANT DISEASES REQUIRING HOSPITALIZATION IN THE INTENSIVE CARE UNIT FOLLOWING HEMATOPOIETIC STEM CELL TRANSPLANTATION AND RISK FACTORS FOR MORTALITY
• STEM CELL TRANSPLANTATIONS FOR PATIENTS WITH FANCONI ANEMIA: AN ISRAELI TERTIARY CENTER EXPERIENCE
• Neurological complications following pediatric allogeneic hematopoietic stem cell transplantation: Risk factors and outcome
• SLP76 Mutation Associated with Combined Immunodeficiency and EBV-Related Lymphoma
• Vedolizumab for pediatric patients with gastrointestinal acute graft-versus-host-disease
• Incremental donor lymphocyte infusion to treat mixed chimerism after allogeneic stem cell transplantation in children with non-malignant diseases
• Two decades of stem cell transplantation in patients with Fanconi anemia: Analysis of factors affecting transplant outcomes
• Development and manufacture of novel locally produced anti-BCMA CAR T cells for the treatment of relapsed/refractory multiple myeloma: results from a phase I clinical trial
• Feasibility of a Novel Academic BCMA-CART (HBI0101) for the Treatment of Relapsed and Refractory AL Amyloidosis
• Clinically Complex LRBA Deficiency Due to a Founder Allele in the Georgian Jewish Population
• Ibrutinib Treatment of Pediatric Chronic Graft-versus-Host Disease: Primary Results from the Phase 1/2 iMAGINE Study
• Clinical and immunophenotypic characteristics of familial leukemia predisposition caused by PAX5 germline variants
• Autoimmune Cytopenias Post Hematopoietic Stem Cell Transplantation in Pediatric Patients With Osteopetrosis and Other Nonmalignant Diseases
• GIMAP6 regulates autophagy, immune competence, and inflammation in mice and humans
• Correction to: Hematopoietic Cell Transplantation Cures Adenosine Deaminase 2 Deficiency: Report on 30 Patients
• Lessons Learned From Five Years of Newborn Screening for Severe Combined Immunodeficiency in Israel
• Preclinical evaluation and structural optimization of anti-BCMA CAR to target multiple myeloma
• Survival of pediatric patients requiring admission in the intensive care unit post hematopoietic stem cell transplantation: Prognostic factors associated with mortality
• Neutrophil decline rate following autologous transplant for lymphoma is a predictor of patients' outcome
• Social determinants of health and primary immunodeficiency
• Clinical presentation and analysis of genotype-phenotype correlations in patients with malignant infantile osteopetrosis
• The expansion of human T-bet^highCD21^low B cells is T cell dependent
• The Clinical Aspect of Adaptor Molecules in T Cell Signaling: Lessons Learnt From Inborn Errors of Immunity
• Hematopoietic Cell Transplantation Cures Adenosine Deaminase 2 Deficiency: Report on 30 Patients
• Evaluation of gastrointestinal symptoms in pediatric patients post hematopoietic stem cell transplantation: Ileo-colonoscopy versus sigmoidoscopy. A single-center experience and review of literature
• Toxicity and efficacy of chimeric antigen receptor T-cell therapy in patients with diffuse large B-cell lymphoma above the age of 70 years compared to younger patients - a matched control multicenter cohort study
• Characterization of a L136P mutation in Formin-like 2 (FMNL2) from a patient with chronic inflammatory bowel disease
• Eltrombopag for enhancement of platelet engraftment in patients undergoing allogeneic cord blood transplantation
• Salvage HLA-haploidentical hematopoietic stem cell transplantation with post-transplant cyclophosphamide for graft failure in non-malignant disorders
• Genomic Spectrum and Phenotypic Heterogeneity of Human IL-21 Receptor Deficiency
• Improved transplant outcomes with myeloablative conditioning for hemophagocytic lymphohistiocytosis in HLA-matched and mismatched donors: a national multicenter retrospective study
• Alternative Splicing of the Inhibitory Immune Checkpoint Receptor SLAMF6 Generates a Dominant Positive Form, Boosting T-cell Effector Functions
• Allogeneic hematopoietic stem cell transplantation in leukocyte adhesion deficiency type I and III